Larotrectinib

Larotrectinib, sold under the brand name Vitrakvi, is a medication for the treatment of cancer.[1][5][7] It is an inhibitor of tropomyosin kinase receptors TrkA, TrkB, and TrkC.Larotrectinib was initially awarded orphan drug status in 2015, for soft tissue sarcoma, and breakthrough therapy designation in 2016 for the treatment of metastatic solid tumors with NTRK fusion.Several earlier drugs, including pembrolizumab, were eventually approved by the FDA for treatment of specific mutations independent of the type of cancer, but those drugs had been initially developed for specific cancer types.[1] Phase II clinical trials evaluating the drug for efficacy and safety in treating several types of solid tumors are ongoing.
Drugs.comMedlinePlusLicense dataDailyMedPregnancycategoryRoutes ofadministrationBy mouthATC codeL01EX12Legal status ℞-only℞-onlyIUPAC nameCAS NumberDrugBankChemSpiderChEMBLCompTox DashboardFormulaMolar massSMILEStropomyosin kinaseArray BioPharmaorphan drug statusbreakthrough therapytissue agnosticpembrolizumabFood and Drug Administrationfirst-in-class medicationTherapeutic Goods AdministrationHealth CanadaEuropean Medicines AgencyClinicalTrials.govTargeted cancer therapyantineoplastic agentsmonoclonal antibodiesReceptor tyrosine kinaseHER1/EGFRCetuximabPanitumumabHER2/neuPertuzumabTrastuzumab+hyaluronidaseTrastuzumab emtansineTrastuzumab deruxtecanZanidatamabCatumaxomabEdrecolomabVEGF-ABevacizumabLeukemialymphomalymphoidGlofitamabElranatamabMosunetuzumabIbritumomabObinutuzumabOfatumumabRituximabTositumomabBrentuximabAlemtuzumabmyeloidGemtuzumab ozogamicinAmivantamabAtezolizumabAvelumabAxatilimabBelantamab mafodotinBermekimabBlinatumomabCemiplimabCosibelimabDaratumumabDinutuximab betaDostarlimabDurvalumabElotuzumabEnfortumab vedotinEpcoritamabInotuzumab ozogamicinIpilimumabIsatuximabLoncastuximab tesirineMirvetuximab soravtansineMogamulizumabMoxetumomab pasudotoxNaxitamabNecitumumabNivolumab+relatlimabOlaratumabOportuzumab monatoxPolatuzumab vedotinRamucirumabRetifanlimabSacituzumab govitecanSerplulimabSugemalimabTafasitamabTalquetamabTarlatamabTeclistamabTislelizumabTisotumab vedotinToripalimabTremelimumabZenocutuzumabZolbetuximabTyrosine kinase inhibitorsAfatinibAumolertinibBrigatinibDacomitinibErlotinibGefitinibIcotinibLazertinibMobocertinibOlmutinibOsimertinibRociletinibVandetanibLapatinibNeratinibTucatinibDabrafenibEncorafenibTovorafenibVemurafenibRTK class IIIAvapritinibAxitinibMasitinibPazopanibRipretinibSorafenibSunitinibToceranibLestaurtinibGilteritinibCediranibFruquintinibLenvatinibNintedanibRegorafenibSemaxanibTivozanibAlectinibCeritinibCrizotinibEnsartinibLorlatinibEntrectinibFutibatinibInfigratinibPemigatinibPralsetinibRepotrectinibSelpercatinibCabozantinibCapmatinibNon-receptorbcr-ablAsciminibBosutinibDasatinibImatinibNilotinibPonatinibRadotinibJanus kinaseBaricitinibFedratinibFilgotinibMomelotinibPacritinibRuxolitinibBinimetinibCobimetinibSelumetinibTrametinibBruton'sAcalabrutinibIbrutinibOrelabrutinibPirtobrutinibZanubrutinibfusion proteinAfliberceptproapoptoticprohibitinAdipotideexotoxinDenileukin diftitoxmTOR inhibitorsEverolimusRidaforolimusSirolimusTemsirolimushedgehogGlasdegibSonidegibVismodegibCDK inhibitorsAbemaciclibDalpiciclibPalbociclibRibociclibTrilaciclibAdagrasibSotorasibPi3K inhibitorsAlpelisibCopanlisibDuvelisibIdelalisibInavolisibParsaclisibRevumenibFibroblast growth factor receptorErdafitinibMidostaurinOdronextamabPexidartinibQuizartinibTebentafuspTepotinibTunlametinibVenetoclaxGrowth factor receptormodulatorsAngiopoietinAngiopoietin 1Angiopoietin 4Angiopoietin 2RebastinibEvinacumabNesvacumabAxokineEGF (ErbB)EGF(ErbB1/HER1)AmphiregulinBetacellulinEGF (urogastrone)EpigenEpiregulinHeparin-binding EGF-like growth factor (HB-EGF)MuroderminNepiderminTransforming growth factor alpha (TGFα)CanertinibGrandininDepatuxizumab mafodotinFutuximabImgatuzumabMatuzumabNimotuzumabZalutumumabErbB2/HER2ErtumaxomabMubritinibErbB3/HER3Neuregulins (heregulins)6 (neuroglycan C)DuligotumabPatritumabSeribantumabErbB4/HER42 (bFGF)10 (KGF2)TraferminPaliferminSpriferminBurosumabFGF15/19HGF (c-Met)FosgonimetonHepatocyte growth factorDihexa (PNB-0408)ForetinibTivantinibVolitinibEmibetuzumabFiclatuzumabFlanvotumabOnartuzumabRilotumumabTelisotuzumab vedotindes(1-3)IGF-1Insulin-like growth factor-1 (somatomedin C)IGF-1 LR3Insulin-like growth factor-2 (somatomedin A)InsulinMecaserminMecasermin rinfabateLinsitinibCixutumumabDalotuzumabFigitumumabGanitumabRobatumumabTeprotumumabDusigitumabTrofinetideLNGF (p75NTR)BNN-20BNN-27CenegerminDHEA-SDexamethasoneTestosteroneFasinumabFrunevetmabFulranumabTanezumabBecaplerminPlatelet-derived growth factorCrenolanibMotesanibTovetumabRET (GFL)GFRα1Glial cell line-derived neurotrophic factor (GDNF)GFRα2Neurturin (NRTN)GFRα3Artemin (ARTN)GFRα4Persephin (PSPN)SCF (c-Kit)AncestimStem cell factorAmitriptylineTavilermide4'-DMA-7,8-DHF7,8-DHF7,8,3'-THFDeoxygeduninDeprenylDiosmetinLM22A-4N-AcetylserotoninNorwogonin (5,7,8-THF)ANA-12Cyclotraxin BGossypetin (3,5,7,8,3',4'-HHF)Placental growth factor (PGF)D (FIGF)PegaptanibAlacizumab pegolIcrucumabRanibizumabAdrenomedullinColony-stimulating factorsConnective tissue growth factor (CTGF)EphrinsErythropoietinGlucose-6-phosphate isomerase (GPI; PGI, PHI, AMF)Glia maturation factor (GMF)Hepatoma-derived growth factor (HDGF)InterleukinsT-cell growth factorsLeukemia inhibitory factor (LIF)Macrophage-stimulating protein (MSP; HLP, HGFLP)Midkine (NEGF2)Migration-stimulating factor (MSF; PRG4)OncomodulinPituitary adenylate cyclase-activating peptide (PACAP)PleiotrophinRenalaseThrombopoietinWnt signaling proteinsCerebrolysinantineoplasticimmunomodulatory