Ridaforolimus

[5] On June 6, 2011, Ariad and Merck announced detailed results from the largest randomized study ever in the soft tissue and bone sarcoma population, the Phase III SUCCEED clinical trial.SUCCEED evaluated oral ridaforolimus, in patients with metastatic soft-tissue or bone sarcomas who previously had a favorable response to chemotherapy.In this patient population, ridaforolimus improved progression-free survival (PFS) compared to placebo, the primary endpoint of the study.Based on 552 progression-free survival (PFS) events in 711 patients, (ridaforolimus (N=347), placebo (N=364) determined by an independent radiological review committee, the study achieved its primary endpoint of improvement in PFS, with a statistically significant (p=0.0001) 28 percent reduction in the risk of progression or death observed in those treated with ridaforolimus compared to placebo (hazard ratio=0.72).Furthermore, based on the full analysis of PFS determined by investigator assessment, there was a statistically significant (p<0.0001) 31 percent reduction by ridaforolimus in the risk of progression or death compared to placebo (hazard ratio=0.69).
ATC codeL01EG03IUPAC nameCAS NumberIUPHAR/BPSChemSpiderChEMBLCompTox DashboardECHA InfoCardFormulaMolar massSMILEScell growthdivisionmetabolismangiogenesissarcomaARIAD PharmaceuticalsNew Drug Applicationchemotherapyprogression-free survivalprimary endpointdouble-blindDiscovery and development of mTOR inhibitorsTargeted cancer therapyantineoplastic agentsmonoclonal antibodiesReceptor tyrosine kinaseHER1/EGFRCetuximabPanitumumabHER2/neuPertuzumabTrastuzumab+hyaluronidaseTrastuzumab emtansineTrastuzumab deruxtecanZanidatamabCatumaxomabEdrecolomabVEGF-ABevacizumabLeukemialymphomalymphoidGlofitamabElranatamabMosunetuzumabIbritumomabObinutuzumabOfatumumabRituximabTositumomabBrentuximabAlemtuzumabmyeloidGemtuzumab ozogamicinAmivantamabAtezolizumabAvelumabAxatilimabBelantamab mafodotinBermekimabBlinatumomabCemiplimabCosibelimabDaratumumabDinutuximab betaDostarlimabDurvalumabElotuzumabEnfortumab vedotinEpcoritamabInotuzumab ozogamicinIpilimumabIsatuximabLoncastuximab tesirineMirvetuximab soravtansineMogamulizumabMoxetumomab pasudotoxNaxitamabNecitumumabNivolumab+relatlimabOlaratumabOportuzumab monatoxPembrolizumabPolatuzumab vedotinRamucirumabRetifanlimabSacituzumab govitecanSerplulimabSugemalimabTafasitamabTalquetamabTarlatamabTeclistamabTislelizumabTisotumab vedotinToripalimabTremelimumabZenocutuzumabZolbetuximabTyrosine kinase inhibitorsAfatinibAumolertinibBrigatinibDacomitinibErlotinibGefitinibIcotinibLazertinibMobocertinibOlmutinibOsimertinibRociletinibVandetanibLapatinibNeratinibTucatinibDabrafenibEncorafenibTovorafenibVemurafenibRTK class IIIAvapritinibAxitinibMasitinibPazopanibRipretinibSorafenibSunitinibToceranibLestaurtinibGilteritinibCediranibFruquintinibLenvatinibNintedanibRegorafenibSemaxanibTivozanibAlectinibCeritinibCrizotinibEnsartinibLorlatinibEntrectinibFutibatinibInfigratinibLarotrectinibPemigatinibPralsetinibRepotrectinibSelpercatinibCabozantinibCapmatinibNon-receptorbcr-ablAsciminibBosutinibDasatinibImatinibNilotinibPonatinibRadotinibJanus kinaseBaricitinibFedratinibFilgotinibMomelotinibPacritinibRuxolitinibBinimetinibCobimetinibSelumetinibTrametinibBruton'sAcalabrutinibIbrutinibOrelabrutinibPirtobrutinibZanubrutinibfusion proteinAfliberceptproapoptoticprohibitinAdipotideexotoxinDenileukin diftitoxmTOR inhibitorsEverolimusSirolimusTemsirolimushedgehogGlasdegibSonidegibVismodegibCDK inhibitorsAbemaciclibDalpiciclibPalbociclibRibociclibTrilaciclibAdagrasibSotorasibPi3K inhibitorsAlpelisibCopanlisibDuvelisibIdelalisibInavolisibParsaclisibRevumenibFibroblast growth factor receptorErdafitinibMidostaurinOdronextamabPexidartinibQuizartinibTebentafuspTepotinibTunlametinibVenetoclaxImmunosuppressive drugsImmunosuppressantsAntimetabolitespurine synthesis inhibitorsAzathioprineMycophenolic aciddihydroorotate dehydrogenaseLeflunomideTeriflunomideantifolateMethotrexateMacrolidesCyclophilinCalcineurinCiclosporinPimecrolimusTacrolimusVoclosporinAbetimusGusperimusLenalidomidePomalidomideThalidomidePDE4 inhibitorApremilastIL-1 receptor antagonistsAnakinraUmirolimusZotarolimusAntibodiesMonoclonalComplement component 5EculizumabAdalimumabAfelimomabCertolizumab pegolGolimumabInfliximabNerelimomabInterleukinBasiliximabBimekizumabBriakinumabBrodalumabCanakinumabDaclizumabGuselkumabIxekizumabOlokizumabRilonaceptRisankizumabSarilumabSatralizumabSecukinumabSiltuximabSirukumabSpesolimabTildrakizumabTocilizumabUstekinumabInterleukin 5MepolizumabImmunoglobulin EOmalizumabInterferonFaralimomabElsilimomabLebrikizumabIL-17AMuromonab-CD3OtelixizumabTeplizumabVisilizumabClenoliximabKeliximabZanolimumabEfalizumabErlizumabOcrelizumabPascolizumabUblituximabGomiliximabLumiliximabTeneliximabToralizumabCD62L/L-selectinAselizumabGaliximabCD147/BasiginGavilimomabFrexalimabRuplizumabBelimumabBertilimumabLerdelimumabMetelimumabIntegrinNatalizumabVedolizumabInterleukin-6 receptorOdulimomabIL-2 receptor/CD25InolimomabT-lymphocyteZolimomab aritoxAnifrolumabAtorolimumabCedelizumabEmapalumabFontolizumabInebilizumabMaslimomabMorolimumabPexelizumabReslizumabRovelizumabSiplizumabTalizumabTelimomab aritoxTeprotumumabVapaliximabVepalimomabPolyclonalAnti-thymocyte globulinAnti-lymphocyte globulinFusionCTLA-4AbataceptBelataceptTNF inhibitorEtanerceptAlefaceptAvacopanBlisibimodCrovalimabDanicopanDarvadstrocelDeucravacitinibDeuruxolitinibDimethyl fumarateDiroximel fumarateEfgartigimod alfaEtrasimodFingolimodIptacopanOzanimodPeficitinibPegcetacoplanPirfenidonePonesimodRavulizumabRitlecitinibRozanolixizumabSiponimodSutimlimabTelitaciceptTofacitinibUpadacitinib